Home Cell Biology Systemic and Local Drug Delivery for Treating Diseases of the Central Nervous System in Rodent Models
Cell Biology JoVE (Open Access) Citable · DOI

Systemic and Local Drug Delivery for Treating Diseases of the Central Nervous System in Rodent Models

DOI: 10.3791/1992-v
What you'll learn
  • Compare systemic drug delivery routes: IV, IP, and oral administration
  • Perform tail vein injection and intraperitoneal injection techniques
  • Execute oral gavage and convection-enhanced delivery procedures
  • Assess drug biodistribution using in vivo imaging methods
Protocol

Biopharma Insights Thorough preclinical testing of drugs that act in the central nervous system often involves assessing and comparing drug biodistribution in association with specific routes of administration. Here, three commonly used methods of systemic delivery (intravenous, intraperitoneal, and oral) as well as a method for local delivery (convection-enhanced delivery) are demonstrated in mice.

Difficulty
intermediate
Total time
~2-3 hours per mouse (depending on imaging endpoints)
Model organism
Mouse
Biosafety
BSL-1

Steps

1
Understand CNS drug delivery routes and rationales

Review the principles of systemic versus local drug administration for CNS therapeutics and the importance of preclinical biodistribution assessment.

▶ 00:31
2
Perform intravenous tail vein injection

Execute tail vein cannulation and drug injection technique in mice, demonstrating proper restraint and vascular access for systemic delivery.

▶ 01:08
3
Administer intraperitoneal injection

Perform IP injection procedure for systemic drug delivery via peritoneal cavity, including proper needle insertion and dosing technique.

▶ 02:49
4
Deliver drug via oral gavage

Execute oral gavage technique using feeding tube for non-invasive systemic drug administration in conscious mice.

▶ 04:01
5
Perform acute convection-enhanced delivery

Conduct stereotaxic brain surgery and convection-enhanced delivery via microinfusion pump for direct local CNS drug administration.

▶ 05:21
6
Acquire in vivo biodistribution imaging

Use imaging modality to visualize and quantify drug distribution across body and brain tissue post-administration.

▶ 09:40
7
Interpret and compare representative results

Analyze biodistribution patterns across delivery routes and discuss relative advantages for CNS drug targeting.

▶ 10:07
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